Some rare diseases that occur in small children are very serious, for the treatment of one such disease, there is a special injection, which costs around Rs 16-18 crore.

Nowadays, most diseases can be treated with medicines, injections, or surgery. However, some diseases are caused by genetic factors and are not so easy to treat. Some rare diseases, especially those affecting young children, are very serious. One such disease is Spinal Muscular Atrophy (SMA), for the treatment of which a special injection is available, which costs around 16-18 crore rupees. It is considered one of the most expensive medicines in the world. So, let us know which small injection costs 16-18 crore rupees and which disease it is used for.

Which small injection costs Rs 16-18 crore?

Zolgensma is a small injection costing ₹16–18 crore (approximately $1.6–1.8 billion). It is considered one of the most expensive medications in the world and is used to treat Spinal Muscular Atrophy (SMA), a serious genetic disease. It is a gene therapy injection. It is typically given to children under the age of 2. It is a one-time injection.

In which diseases is it used?

Zolgensma, a small injection costing ₹16–18 crore, is used to treat Spinal Muscular Atrophy (SMA). SMA is a genetic neuromuscular disorder that affects the body's nerves and muscles. In this condition, the motor neurons, which control muscles, don't function properly. In this condition, a gene called SMN1 is damaged or missing, resulting in the production of a crucial protein.

This causes the child's muscles to gradually weaken. They have difficulty sitting, standing, or walking. In severe cases, breathing and swallowing may also become difficult. In SMA, an important gene (SMN1) in the child's body doesn't function properly. Zolgensma replaces the faulty gene with a copy of the correct gene, which can improve muscle strength.

What are its symptoms?

Symptoms of SMA can vary from child to child, but some common signs include a child's inability to sit or walk on time, weak limbs, difficulty supporting their head, fatigue, and difficulty breathing or swallowing. If these symptoms occur, it's important to consult a doctor immediately.

Disclaimer: This information is based on research studies and expert opinion. Do not substitute for medical advice. Always consult your doctor or relevant specialist before undertaking any new activity or exercise.

PC:ABPNews